Targeted therapy improves cellular dysfunction, ataxia, and seizure susceptibility in a model of a progressive myoclonus epilepsy
- Huijie Feng
- , Jerome Clatot
- , Keisuke Kaneko
- , Marco Flores-Mendez
- , Eric R. Wengert
- , Carly Koutcher
- , Emily Hoddeson
- , Emily Lopez
- , Demetrius Lee
- , Leroy Arias
- , Qiansheng Liang
- , Xiaohong Zhang
- , Ala Somarowthu
- , Manuel Covarrubias
- , Martin J. Gunthorpe
- , Charles H. Large
- , Naiara Akizu
- , Ethan M. Goldberg
Research output: Contribution to journal › Article › peer-review
8
Citations
(Scopus)